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Spinal Muscular Atrophy – final stages of development of a treatment

Reading Time: 2 minutes In the Sheffield Institute for Translational Neuroscience (SITraN), the gene therapy group led by Prof Mimoun Azzouz is approaching the final stages of preclinical development of a treatment for Spinal Muscular Atrophy (a childhood disease of the motor neurones). Here Chris Binny explains more about the group’s work. About Spinal Muscular Atrophy Spinal muscular atrophy…

Understanding Spinal Muscular Atrophy: could plant derived compounds hold the key?

Reading Time: 3 minutes On 3 March 2014, researchers based at the University of Edinburgh published a research paper that extends our understanding of the childhood disease – Spinal Muscular Atrophy (SMA). Although this is not MND so-to-speak, the disease does affect the motor neurones. Plus, the results were so interesting; I couldn’t resist writing a blog post about them.…