An ASO is a short synthetic single strand of DNA that targets a specific region of a gene that produces a faulty protein known to cause disease. It can reduce production of that faulty protein or stop it from being expressed completely, or restore function to that protein.
Antisense oligonucleotide
Kiran
I work as a Senior Research Officer within the MND Association to communicate the latest updates in MND research across our platforms. Additionally, I manage the digital platforms and communications for the International Symposium on ALS/MND. I graduated with a master's degree in Neuroscience from Cardiff University in 2023. I have previously supported the awareness of Fragile X syndrome within the UK.