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Spinal Muscular Atrophy – final stages of development of a treatment

Reading Time: 3 minutes In the Sheffield Institute for Translational Neuroscience (SITraN), the gene therapy group led by Prof Mimoun Azzouz is approaching the final stages of preclinical development of a treatment for Spinal Muscular Atrophy (a childhood disease of the motor neurones). Here Chris Binny explains more about the group’s work. About Spinal Muscular Atrophy Spinal muscular atrophy…